Medical Xpress

Musculoskeletal Diseases: News and Research on Muscular Dystrophies

If cancer is a disease of overabundance, where cells divide without restraint and tumors grow despite the body's best interests, then degenerative diseases are disorders of deprivation. When ...
Business Insider

Muscular Dystrophy Association Announces nearly $2 Million in Collaborative Research Grants Advancing Treatments Across Multiple Neuromuscular Diseases

New York, Dec. 03, 2025 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) today announced the awarding of seven new collaborative research grants totaling nearly $2 million to advance ...
Morningstar

Cure Rare Disease Awarded $7.4 Million CIRM Grant to Advance Gene Therapy for Limb-Girdle Muscular Dystrophy Type 2i/R9

Cure Rare Disease (CRD) announced it has been awarded a $7.4 million grant from the California Institute for Regenerative Medicine (CIRM) to advance the development of a novel gene therapy for ...
Nasdaq

Capricor Therapeutics Receives Orphan Drug Designation for Deramiocel in Becker Muscular Dystrophy, Expanding Focus in Neuromuscular Diseases

Capricor Therapeutics announced that the U.S. FDA has granted Orphan Drug Designation to its lead cell therapy candidate, Deramiocel, for the treatment of Becker Muscular Dystrophy (BMD). This ...
EurekAlert!

Genethon signs licensing agreement with AskBio for the development of an investigational gene therapy for Pompe disease

Genethon, a leading laboratory in gene therapy for rare diseases, today announced that it has entered into an exclusive, worldwide licensing agreement with AskBio, a gene therapy company wholly owned ...